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In this Episode:

• You Got This, Mental Health – Feeling seen and heard.  Some of the responsibilty is on you.
• Can a single person make a difference? The amazing story of the first approved drug for Friedreich’s ataxia (FA)
• Thank you notes – Reata Pharmaceuticals, and Kyle’s landlord at work.

As the story goes, a concerned mother, in an effort to do whatever she could for her son who has Friedreich’s ataxia (FA), connected a few important dots about science and the pharmaceutical industry.  When she decided to make a phone call to the Friedreich’s Ataxia Research Alliance (FARA), she started a series of actions and events that eventually led to the approval of the first treatment for FA, SKYCLARYS.  Listen for the details.

Links and Resources:

• Announcement: First Medication to Treat Friedreich’s Ataxia Approved on Rare Disease Day!